He added: “Great Ormond Street told us they couldn’t find a bone marrow match so they offered the gene therapy, I said ‘if that’s the only option they have, we have to do it’.

He added: “Great Ormond Street told us they couldn’t find a bone marrow match so they offered the gene therapy, I said ‘if that’s the only option they have, we have to do it’. “Since then, because of ...

Martin Mwita, 20, is the first patient in St. Louis and among the first across the country to receive a new gene therapy for ...

The main treatment strategies being explored are gene therapy, fibroblast cell therapy, bone marrow stem cell therapy, and protein therapy, with gene therapy appearing the most promising for RDEB.

Vertex Pharma's £1.65 million ($2.05 million) gene-editing therapy for sickle cell disease ... who might otherwise be treated using a bone marrow transplant, but have no suitable donor available.

Data from the first patients enrolled into Regenxbio's trial of its gene therapy for rare inherited ... chemotherapy to destroy the patient's bone marrow. The latest readout is a boost for ...

Advani (Padma Shri, Padma Bhushan), announced the opening of a Centre of Excellence in CAR T-Cell Therapy and Bone Marrow Transplantation at Smita ... globally benchmarked cell and gene therapies to ...