Ask scientists which gene-editing tool is most needed to advance gene therapy, and they'd probably describe a system that's ...

Once prostate cancer no longer responds to hormonal therapy, the cancer is called castration-resistant. Find out which ...

A CRISPR treatment seems to have been effective for a baby’s devastating disease, but it is not clear whether such bespoke ...

The UNC technology, developed by Pediatrics Professor Chengwen Li, M.D., Ph.D., uses adeno-associated viruses (AAVs) to ferry ...

Early detection of retinoblastoma can save children’s lives and vision. AIIMS Delhi stresses awareness, timely care, genetic ...

FDA grants accelerated approval to AbbVie's Emrelis for c-Met overexpressing NSCLC; siRNA partnership with ADARx includes ...

May 15, 2025 — A research team has developed and safely delivered a personalized gene editing therapy to treat an infant with a life-threatening, incurable genetic disease. The infant, who was ...

Two research articles published in Nature Genetics shed new light on the cellular complexity of glioblastoma, the most ...

GEN2 is well tolerated with minimal toxicity and signs of pharmacodynamic activity in an ongoing Phase 1 dose escalation and ...

In cancer cases, while the patients with advanced conditions lose appetite, doctors say, the body needs more nutrition for ...

To address this challenge, CTMC has established a patient material bank, enabling early-stage process development with clinically relevant samples. This resource also supports continuous process ...