Stocktwits - Shares of gene therapy developer uniQure N.V. (QURE) shot up 41% on Thursday afternoon after it announced that the U.S. Food and Drug Administration (FDA) has granted Breakthrough Therapy ...

Advani (Padma Shri, Padma Bhushan), announced the opening of a Centre of Excellence in CAR T-Cell Therapy and Bone Marrow Transplantation at Smita ... globally benchmarked cell and gene therapies to ...

Marks fourth FDA designation for ATSN-201, which has also received Fast Track, Rare Pediatric Disease and Orphan Drug Designations DURHAM, N.C., April 15, 2025 (GLOBE NEWSWIRE) -- Atsena Therapeutics, ...

Japanese pharmaceutical company Takeda and domestic biotech company Belief BioMed jointly announced on Thursday that the gene therapy drug Dalnacogene Ponparvovec Injection has received approval ...

Loma Linda University Health is the first hospital in Southern California to deliver the groundbreaking FDA-approved gene therapy. “I'll be there for her until my last breath. As long as I have ...

BBM-H901 is the first gene therapy approved for haemophilia B in China. Credit: angellodeco/Shutterstock. Belief BioMed (BBM) and Takeda China have announced China ...

In May 2018, North Carolina awarded the Novartis gene therapy division (then called AveXis, later renamed Novartis Gene Therapies) an initial job development investment grant to build a new ...

Simon is Professor of Gene Therapy at University College London. Over the past two decades he has worked on treatments for muscular dystrophy, cystic fibrosis, haemophilia and thalassemia; more ...

Bluebird Bio and Xcellbio have entered into an agreement to support the commercialization of Lyfgenia (lovotibeglogene autotemcel), Bluebird’s gene therapy for sickle cell ... stem cells from a ...

Get Instant Summarized Text (Gist) Gene therapy for Duchenne muscular dystrophy (DMD) faces challenges as the immune system may hinder its effectiveness. A large-scale trial showed that the ...

What is a bone marrow test? A bone marrow test is a way of testing cells from your bone marrow. Bone marrow is the spongy tissue inside your bones that makes blood cells. To find out whether there are ...

Myelosuppression, or bone marrow suppression, is defined as a decrease in the ability of the bone marrow to produce blood cells. This may result in a lack of red blood cells (anemia), white blood ...