Marley Mansour was diagnosed in early 2023 after years of unanswered questions. The rare genetic disorder affects protein ...

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A protein was created where TDP-43 was fused to the SUMO2 protein and these fusion proteins were expressed in cells with or ...

Scientists are placing greater emphasis on both the genetic blueprint and therapies that target genes as the most effective methods to target the root cause of disease. Medical technologies are ...

This year's Futures National Conference, hosted by CureDuchenne for the Duchenne and Becker MD communities, is scheduled to ...

Novavax has been available since 2022 through a pandemic-era Emergency Use Authorization. A decision on full approval – which ...

The Department of Health and Human Services, which oversees FDA and other health agencies, did not immediately respond to a ...

AMX0114 is an antisense oligonucleotide made to prevent or slow the degeneration of axons, which is a key driver of ALS ...

The goal of the HMS Initiative for RNA Medicine is to make and translate RNA discoveries into novel therapeutics and diagnostics by fostering a climate of outstanding basic, translational and clinical ...

Copyright 2025 The Associated Press. All Rights Reserved. Copyright 2025 The Associated Press. All Rights Reserved. Former Rep. Barbara Lee makes her first public ...

Progressive icon and former U.S. Rep. Barbara Lee is the new mayor of troubled Oakland, California, a city she represented for more than two decades in Congress SAN FRANCISCO -- Progressive icon ...

MacLean is going strong at 65 on the TV institution he has defined for almost four decades: 'It hasn't been a smooth ride, but it's a good ride' You can save this article by registering for free ...