Sebastien Beauzile became the first person in NY to be made symptom-free after undergoing a new type of gene therapy.

Somatic gene therapy targets non-reproductive cells in the body, such as bone marrow, blood cells, or liver cells. The genetic modifications are limited to the treated individual and are not inherited ...

To date, the therapeutic results of gene therapy have been marginal ... adult stem cell therapies have been transplantations of bone marrow and peripheral blood stem cells to treat cancers ...