As we continue to see sequencing technologies advance and provide a deeper understanding of gene therapy targets along with ...

A Minnesota woman was told her stage 4 colon cancer couldn’t be cured. Two years later, she’s cancer-free — and says a ...

An infant with a severe genetic condition has shown signs of improvement after receiving a gene-editing treatment tailored to ...

Ask scientists which gene-editing tool is most needed to advance gene therapy, and they'd probably describe a system that's ...

The UNC technology, developed by Pediatrics Professor Chengwen Li, M.D., Ph.D., uses adeno-associated viruses (AAVs) to ferry ...

Researchers have completed a first-in-human clinical trial testing a CRISPR/Cas9 gene-editing technique to help the immune system fight advanced gastrointestinal (GI) cancers. The results show ...

May 15, 2025 — A research team has developed and safely delivered a personalized gene editing therapy to treat an infant with a life-threatening, incurable genetic disease. The infant, who was ...

Ask scientists what gene editing tool is most needed to advance gene therapy, and they'd probably describe a system that's now close to realization in the labs of Samuel Sternberg at Columbia ...

To address this challenge, CTMC has established a patient material bank, enabling early-stage process development with clinically relevant samples. This resource also supports continuous process ...

Instead of killing all fast-growing cells or keeping them from dividing, targeted therapies work more selectively against cancer cells. They do one of three things: They target a gene or protein that ...

Once prostate cancer no longer responds to hormonal therapy, the cancer is called castration-resistant. Find out which ...